Rare Disease-Focused-Ultragenyx Pharmaceutical Stock Falls On Serious Adverse Events In Eaarly Genetic Disorder Study
New data from Phase 1/2 study of GTX-102 for Angelman syndrome shows rapid and sustained improvement in patients, exceeding natural history data. read more.....»»
Tackling deadly newborn disease, BridgeBio affiliate wins FDA drug approval
The BridgeBio model is designed to move drugs tackling rare diseases with a well-defined genetic basis quickly and efficiently to approval......»»
Small Peninsula biotech targets big impact on deadly childhood aging disease
Working with a patient organization, Palo Alto company aims for big impact on a childhood genetic disease that often kills kids by 15......»»
Mustang Bio Gallops Higher On Positive Gene Therapy Results For Deadly "Bubble Boy Disease"
Shares of Mustang Bio Inc (NASDAQ: MBIO) are skyrocketing to their highest level in about a year Thursday morning. read more.....»»
St. Jude develops cure for ‘bubble boy’ disease
A disease made well-known by John Travolta and a 1976 TV movie has been cured in Memphis. St. Jude Children's Research Hospital has cured 10 children with SCID-X1 — commonly known as "bubble boy" disease — who, until now, would not have lived .....»»
Can the Gene-Editing Technology CRISPR Cure This Debilitating Brain Disease?
Is CRISPR the miracle we've been hoping for to treat genetic brain diseases?.....»»
Scientists have found a way to calculate your risk for deadly conditions like diabetes, breast cancer and heart disease
Flickr/Micah Baldwin A new genetic test which can test how likely a person is to contract serious conditions like heart disease and diabetes has been developed, according to a st.....»»
Column: California"s stem cell program found a disease cure, but it"s being blocked by a biotech firm
A biotech firm has halted work on a state-funded disease cure, purely for its bottom line.A biotech firm has halted work on a state-funded disease cure, purely for its bottom line......»»
India"s COVID-19 Crisis Leads To Black Market Price Explosion
India's COVID-19 Crisis Leads To Black Market Price Explosion India recorded another 320,000 Covid-19 infections on Tuesday as the country struggles to cope with a deadly surge of the disease. H.....»»
Bluebird Bio provides update on severe genetic disease programs and business ops
See the rest of the story here. Theflyonthewall.com provides the latest financial news as it breaks. Known as a leader in market intelligence, The Fl.....»»
The Deadly Pig Virus That’s Proving Difficult to Beat
A deadly swine disease that’s plagued pig farmers for years is re-emerging across Asia, illustrating how difficult African swine.....»»
BridgeBio Pharma Gets First FDA-Approval For Rare Genetic Metabolic Disorder
BridgeBio Pharma Inc (NASDAQ: BBIO) and affiliate Origin Biosciences Inc have received the read more.....»»
Translating passion into execution: Cure Rare Disease"s founder on the business of biotech
When a career path chooses you in the form of a pressing personal cause, passion and commitment must soon be followed by execution. And that means schooling up — quickly. I had heard the call of entrepreneurship early. I had a new Harvard B.....»»
Genetic Technologies provides update on COVID-19 disease severity risk test
See the rest of the story here. Theflyonthewall.com provides the latest financial news as it breaks. Known as a leader in market intelligence, The Fl.....»»
JPMorgan revenue spikes as COVID-19 relief soothes economic pain
Congressional action on a second coronavirus-relief package and the development of vaccines to treat the deadly disease enabled the lender to free $2.9 billion in loan reserves.....»»
Bluebird"s stock is up 5% as it details plans to separate oncology and genetic disease businesses
Shares of Bluebird Bio Inc. gained 5.1% in premarket trading on Monday after it announced plans to spin off its oncology business as a separate publicly-traded company. Bluebird will retain its genetic disease business. Bluebir.....»»
The most common coronavirus symptoms in children — and how to know if they have a rare post-virus inflammatory syndrome
Getty Young people seem to be less vulnerable than older populations to the coronavirus, and tend to experience mild symptoms when they do get it. But reports of a poorly-understood and deadly inflammatory disease.....»»
North Carolina drugmaker Chimerix may have treatment for coronavirus — and another for smallpox
A Triangle drugmaker is beginning trials for a potential treatment for Covid-19, while at the same time the company is close to locking down a federal contract to stockpile treatments for another deadly disease......»»
Hundreds of "patriots" volunteer for Bay Area program to help startups defeat COVID
Health Hub focuses on digital health and the future of health care, but it with all eyes on COVID-19 moved to link its volunteer advisors to startups looking to attack the deadly disease.....»»
Hundreds of "patriots" volunteer for UCSF-related program to help startups defeat COVID
Health Hub focuses on digital health and the future of health care, but it with all eyes on COVID-19 moved to link its volunteer advisors to startups looking to attack the deadly disease.....»»